GeneticsFebruary 15, 2022
First Gene Therapy for Tay-Sachs Disease Successfully Given to Two Children
About one in 300 people in the general population carry the Tay-Sachs disease gene
Stories by Miguel Sena-Esteves
Miguel Sena-Esteves is an associate professor of neurology and a member of the Horae Gene Therapy Center. Sena-Esteves received his PhD in biomedical sciences from the University of Porto, Portugal, where he started his work in gene therapy.