Gene therapy

Scientists try to understand why some patients get better and others don't

The gene editing method called CRISPR is already used in the lab to insert and remove genome defects in animal embryos

Whenever one examines any area of scientific inquiry, there are two important things to understand: where the science is today, and where it may lead us in the future.

By tweaking the charges of brain cells, researchers alter early brain development, opening a door to healing mature brains or undoing genetic damage

White House’s move to develop customized care prompts worries about data security and informed consent

Repairing the faulty genes that cause haemophilia could ultimately cure the disease, but it will be a tough challenge

History explains why people with the malady, and their physicians, are cautious to believe that a cure is in sight

A promising therapy curtails clotting inhibitors rather than replacing proteins that promote blood clotting

Hairlike structures on cells may play a role in a host of genetic disorders, including kidney degeneration, vision impairment and even some cancers

Hormone and gene therapies for anxiety and PTSD could be on the way

A DNA-editing technique based on bacterial “memories” could revolutionize medicine. But some worry it could get out of control

DNA-based memory can record multiple inputs from engineered gene circuits